University of Virginia School of Medicine scientists have used a next-generation form of gene editing to fix the underlying cause of a severe form of epilepsy in lab mice.

You may have seen it in the news recently: a baby in Pennsylvania with a rare genetic disorder was healed with a personalized treatment that repaired his specific genetic mutation. The treatment was ...

A collaboration between scientists at the Institute of Molecular and Clinical Ophthalmology Basel (IOB) and Beam Therapeutics has resulted in a new base editing therapy for Stargardt disease, the most ...

University of Virginia School of Medicine researchers have used an advanced gene-editing technique to correct the underlying ...

Researchers at the Broad Institute of MIT and Harvard have developed a gene-editing treatment for prion disease that extends lifespan by about 50 percent in a mouse model of the fatal ...

X-linked chronic granulomatous disease (X-CGD) is a rare genetic disorder characterized by high susceptibility to infections that results from genetic mutations in the cytochrome b-245 beta chain ...

Forbes contributors publish independent expert analyses and insights. Juergen Eckhardt leads Bayer’s impact investment unit, Leaps by Bayer. Dr. David Liu, pictured with former lab members Holly Rees ...

Base editors are a type of gene editing tool designed to make precise changes to DNA at the single-nucleotide level. They are used to correct genetic variants that cause disease. 1 This article ...

Beam is now in the strongest position of all companies advancing a genetic therapy for alpha-1 antitrypsin deficiency, ...

Durable expression of anti-sickling fetal hemoglobin and reduction in sickle hemoglobin ob ...